Efficient and safe therapeutic use of paired Cas9-nickases for primary hyperoxaluria type 1

  1. Torella, L.
  2. Klermund, J.
  3. Bilbao-Arribas, M.
  4. Tamayo, I.
  5. Andrieux, G.
  6. Chmielewski, K.O.
  7. Vales, A.
  8. Olagüe, C.
  9. Moreno-Luqui, D.
  10. Raimondi, I.
  11. Abad, A.
  12. Torrens-Baile, J.
  13. Salido, E.
  14. Huarte, M.
  15. Hernaez, M.
  16. Boerries, M.
  17. Cathomen, T.
  18. Zabaleta, N.
  19. Gonzalez-Aseguinolaza, G.
Journal:
EMBO molecular medicine

ISSN: 1757-4684

Year of publication: 2024

Volume: 16

Issue: 1

Pages: 112-131

Type: Article

DOI: 10.1038/S44321-023-00008-8 GOOGLE SCHOLAR lock_openOpen access editor

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