AAV4Cancer
Terapias Avanzadas para Enfermedades Hepáticas Raras
Publications (2) Publications in which a researcher has participated
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Cellular and Molecular Neuroscience
2021
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Glucocerebrosidase gene therapy induces alpha-synuclein clearance and neuroprotection of midbrain dopaminergic neurons in mice and macaques
International Journal of Molecular Sciences, Vol. 22, Núm. 9
2020
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Inhibition of microRNA 6937 delays photoreceptor and vision loss in a mouse model of retinitis pigmentosa
Pharmaceutics, Vol. 12, Núm. 10, pp. 1-15