Disease pharmacokinetic–pharmacodynamic modelling in acute intermittent porphyria to support the development of mRNA-based therapies

1. Parra-Guillen, Z.P.
2. Fontanellas, A.
3. Jiang, L.
4. Jericó, D.
5. Martini, P.
6. Vera-Yunca, D.
7. Hard, M.
8. Guey, L.T.
9. Troconiz, I.F.