AAV-PHP.B-Mediated Global-Scale Expression in the Mouse Nervous System Enables GBA1 Gene Therapy for Wide Protection from Synucleinopathy

  1. Morabito, G.
  2. Giannelli, S.G.
  3. Ordazzo, G.
  4. Bido, S.
  5. Castoldi, V.
  6. Indrigo, M.
  7. Cabassi, T.
  8. Cattaneo, S.
  9. Luoni, M.
  10. Cancellieri, C.
  11. Sessa, A.
  12. Bacigaluppi, M.
  13. Taverna, S.
  14. Leocani, L.
  15. Lanciego, J.L.
  16. Broccoli, V.
Journal:
Molecular Therapy

ISSN: 1525-0024 1525-0016

Year of publication: 2017

Volume: 25

Issue: 12

Pages: 2727-2742

Type: Article

DOI: 10.1016/J.YMTHE.2017.08.004 GOOGLE SCHOLAR lock_openOpen access editor