Use of an adeno-associated virus serotype Anc80 to provide durable cure of phenylketonuria in a mouse model

  1. Kaiser, R.A.
  2. Weber, N.D.
  3. Trigueros-Motos, L.
  4. Allen, K.L.
  5. Martinez, M.
  6. Cao, W.
  7. VanLith, C.J.
  8. Hillin, L.G.
  9. Douar, A.
  10. González-Aseguinolaza, G.
  11. Aldabe, R.
  12. Lillegard, J.B.
Journal:
Journal of Inherited Metabolic Disease

ISSN: 1573-2665,  0141-8955

Year of publication: 2021

Volume: 44

Issue: 6

Pages: 1369-1381

Type: Article

DOI: 10.1002/JIMD.12392 GOOGLE SCHOLAR lock_openOpen access editor
Data source: Scopus