Gene therapy for progressive familial intrahepatic cholestasis type 3 in a clinically relevant mouse model
- Weber, N.D.
- Odriozola, L.
- Martínez-García, J.
- Ferrer, V.
- Douar, A.
- Bénichou, B.
- González-Aseguinolaza, G.
- Smerdou, C.
Journal:
Nature Communications
ISSN: 2041-1723
Year of publication: 2019
Volume: 10
Issue: 1
Type: Article