Publicaciones en colaboración con investigadores/as de Centro de Regulación Genómica (2)

2013

  1. In vitro correction of a pseudoexon-generating deep intronic mutation in LGMD2A by antisense oligonucleotides and modified small nuclear RNAs

    Human Mutation, Vol. 34, Núm. 10, pp. 1387-1395

2012

  1. AAV vectors transduce hepatocytes in vivo as efficiently in cirrhotic as in healthy rat livers

    Gene Therapy, Vol. 19, Núm. 4, pp. 411-417