Publicaciones en colaboración con investigadores/as de University of Paris-Sorbonne (2)

2024

  1. Systemic messenger RNA replacement therapy is effective in a novel clinically relevant model of acute intermittent porphyria developed in non-human primates

    Gut

2021

  1. Add-on cannabidiol in patients with Dravet syndrome: Results of a long-term open-label extension trial

    Epilepsia, Vol. 62, Núm. 10, pp. 2505-2517