Hepatología: Metabolismo, Epigenética y Carcinogénesis
METACAN
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German Cancer Research Center
Heidelberg, AlemaniaPublications en collaboration avec des chercheurs de German Cancer Research Center (2)
2016
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Phase I open label liver-directed gene therapy clinical trial for acute intermittent porphyria
Journal of Hepatology, Vol. 65, Núm. 4, pp. 776-783
2013
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Safety and liver transduction efficacy of raav5-cohpbgd in nonhuman primates: A potential therapy for acute intermittent porphyria
Human Gene Therapy, Vol. 24, Núm. 12, pp. 1007-1017