Terapias Avanzadas para Enfermedades Hepáticas Raras
AAV4Cancer
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Children's Hospitals and Clinics of Minnesota
Saint Paul, Estados UnidosPublicaciones en colaboración con investigadores/as de Children's Hospitals and Clinics of Minnesota (1)
2021
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Use of an adeno-associated virus serotype Anc80 to provide durable cure of phenylketonuria in a mouse model
Journal of Inherited Metabolic Disease, Vol. 44, Núm. 6, pp. 1369-1381