Terapia Génica para Encefalopatías Congénitas
Instituto de Investigación Sanitaria de Navarra
Pamplona, EspañaPublicaciones en colaboración con investigadores/as de Instituto de Investigación Sanitaria de Navarra (16)
2023
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Engineering U1-Based Tetracycline-Inducible Riboswitches to Control Gene Expression in Mammals
ACS Nano, Vol. 17, Núm. 23, pp. 23331-23346
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Preferential expression of SCN1A in GABAergic neurons improves survival and epileptic phenotype in a mouse model of Dravet syndrome
Journal of Molecular Medicine, Vol. 101, Núm. 12, pp. 1587-1601
2022
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Galectin-3 inhibition boosts the therapeutic efficacy of Semliki Forest virus in pediatric osteosarcoma
Molecular Therapy - Oncolytics, Vol. 26, pp. 246-264
2021
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Adenovirus-mediated inducible expression of a pd-l1 blocking antibody in combination with macrophage depletion improves survival in a mouse model of peritoneal carcinomatosis
International Journal of Molecular Sciences, Vol. 22, Núm. 8
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AdrA as a Potential Immunomodulatory Candidate for STING-Mediated Antiviral Therapy That Required Both Type I IFN and TNF-α Production
Journal of immunology (Baltimore, Md. : 1950), Vol. 206, Núm. 2, pp. 376-385
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Local administration of IL-12 with an HC vector results in local and metastatic tumor control in pediatric osteosarcoma
Molecular Therapy - Oncolytics, Vol. 20, pp. 23-33
2019
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Short-Term Local Expression of a PD-L1 Blocking Antibody from a Self-Replicating RNA Vector Induces Potent Antitumor Responses
Molecular Therapy, Vol. 27, Núm. 11, pp. 1892-1905
2018
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Brain copper storage after genetic long-term correction in a mouse model of Wilson disease
Neurology: Genetics, Vol. 4, Núm. 3
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Inhibition of adenovirus infection by mifepristone
Antiviral Research, Vol. 159, pp. 77-83
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Visualization of the therapeutic efficacy of a gene correction approach in Wilson's disease by laser-ablation inductively coupled mass spectrometry
Journal of Hepatology
2017
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X-box Binding Protein 1 Regulates Unfolded Protein, Acute-Phase, and DNA Damage Responses During Regeneration of Mouse Liver
Gastroenterology, Vol. 152, Núm. 5, pp. 1203-1216.e15
2016
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A versatile vector for in vivo monitoring of type I interferon induction and signaling
PLoS ONE, Vol. 11, Núm. 3
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Capsid-deficient alphaviruses generate propagative infectious microvesicles at the plasma membrane
Cellular and Molecular Life Sciences, Vol. 73, Núm. 20, pp. 3897-3916
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Gene therapy approaches against cancer using in vivo and ex vivo gene transfer of interleukin-12
Immunotherapy, Vol. 8, Núm. 2, pp. 179-198
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Long-term metabolic correction of Wilson's disease in a murine model by gene therapy
Journal of Hepatology, Vol. 64, Núm. 2, pp. 419-426