Terapia Génica para Encefalopatías Congénitas
Clínica Universitaria de Navarra
Pamplona, EspañaPublicaciones en colaboración con investigadores/as de Clínica Universitaria de Navarra (21)
2023
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Preferential expression of SCN1A in GABAergic neurons improves survival and epileptic phenotype in a mouse model of Dravet syndrome
Journal of Molecular Medicine, Vol. 101, Núm. 12, pp. 1587-1601
2022
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Oncolytic DNX-2401 Virus for Pediatric Diffuse Intrinsic Pontine Glioma
New England Journal of Medicine, Vol. 386, Núm. 26, pp. 2471-2481
2021
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Author Correction: Epilepsy and neuropsychiatric comorbidities in mice carrying a recurrent Dravet syndrome SCN1A missense mutation (Scientific Reports, (2019), 9, 1, (14172), 10.1038/s41598-019-50627-w)
Scientific Reports
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Transfer of SCN1A to the brain of adolescent mouse model of Dravet syndrome improves epileptic, motor, and behavioral manifestations
Molecular Therapy - Nucleic Acids, Vol. 25, pp. 585-602
2019
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Epilepsy and neuropsychiatric comorbidities in mice carrying a recurrent Dravet syndrome SCN1A missense mutation
Scientific Reports, Vol. 9, Núm. 1
2017
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X-box Binding Protein 1 Regulates Unfolded Protein, Acute-Phase, and DNA Damage Responses During Regeneration of Mouse Liver
Gastroenterology, Vol. 152, Núm. 5, pp. 1203-1216.e15
2016
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Capsid-deficient alphaviruses generate propagative infectious microvesicles at the plasma membrane
Cellular and Molecular Life Sciences, Vol. 73, Núm. 20, pp. 3897-3916
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Long-term metabolic correction of Wilson's disease in a murine model by gene therapy
Journal of Hepatology, Vol. 64, Núm. 2, pp. 419-426
2015
2013
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Cytokines for the treatment of gastrointestinal cancers: Clinical experience and new perspectives
Expert Opinion on Investigational Drugs, Vol. 22, Núm. 7, pp. 827-841
2012
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Evaluation of monocytes as carriers for armed oncolytic adenoviruses in murine and Syrian hamster models of cancer
Human Gene Therapy, Vol. 23, Núm. 12, pp. 1258-1268
2011
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Gene therapy of liver cancer: An update
Journal Africain du Cancer, Vol. 3, Núm. 3, pp. 180-192
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Oxaliplatin in combination with liver-specific expression of interleukin 12 reduces the immunosuppressive microenvironment of tumours and eradicates metastatic colorectal cancer in mice
Gut, Vol. 60, Núm. 3, pp. 341-349
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Self-inactivating helper virus for the production of high-capacity adenoviral vectors
Gene Therapy, Vol. 18, Núm. 11, pp. 1025-1033
2009
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Deletion of the E3-6.7K/gp19K region reduces the persistence of wild-type adenovirus in a permissive tumor model in Syrian hamsters
Cancer Gene Therapy, Vol. 16, Núm. 9, pp. 703-712
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Evaluation of bioluminescent imaging for noninvasive monitoring of colorectal cancer progression in the liver and its response to immunogene therapy
Molecular Cancer, Vol. 8
2008
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Interleukin-12 inhibits liver-specific drug-inducible systems in vivo
Gene Therapy, Vol. 15, Núm. 4, pp. 277-288
2007
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Gene therapy of liver cancer
Annals of Hepatology, Vol. 6, Núm. 1, pp. 5-14
2006
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Recombinant Adenoviral Vectors Turn on the Type I Interferon System without Inhibition of Transgene Expression and Viral Replication
Molecular Therapy, Vol. 14, Núm. 1, pp. 129-138
2005
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In utero gene therapy: Current challenges and perspectives
Molecular Therapy, Vol. 11, Núm. 5, pp. 661-676