Terapia Génica para Encefalopatías Congénitas
Great Ormond Street Hospital for Children NHS Foundation Trust
Londres, Reino UnidoPublicacions en col·laboració amb investigadors/es de Great Ormond Street Hospital for Children NHS Foundation Trust (1)
2022
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Preclinical model for phenotypic correction of dystrophic epidermolysis bullosa by in vivo CRISPR-Cas9 delivery using adenoviral vectors
Molecular Therapy - Methods and Clinical Development, Vol. 27, pp. 96-108