Juan Roberto
Rodríguez Madoz
Profesional Investigador
Centro de Investigación Médica Aplicada
Pamplona, EspañaPublicacións en colaboración con investigadores/as de Centro de Investigación Médica Aplicada (36)
2024
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Rna-loaded nanoparticles for the treatment of hematological cancers
Advanced Drug Delivery Reviews, Vol. 214
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Tethered IL15-IL15Rα augments antitumor activity of CD19 CAR-T cells but displays long-term toxicity in an immunocompetent lymphoma mouse model
Journal for immunotherapy of cancer, Vol. 12, Núm. 7
2023
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FOXP3 expression diversifies the metabolic capacity and enhances the efficacy of CD8 T cells in adoptive immunotherapy of melanoma
Molecular Therapy, Vol. 31, Núm. 1, pp. 48-65
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Optimization of universal allogeneic CAR-T cells combining CRISPR and transposon-based technologies for treatment of acute myeloid leukemia
Frontiers in Immunology, Vol. 14
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Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDi
Molecular Therapy Nucleic Acids, Vol. 34
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Revealing cell populations catching the early stages of human embryo development in naive pluripotent stem cell cultures
Stem Cell Reports, Vol. 18, Núm. 1, pp. 64-80
2022
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CAR density influences antitumoral efficacy of BCMA CAR T cells and correlates with clinical outcome
Science Advances, Vol. 8, Núm. 39
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Generation of NKX2.5GFP Reporter Human iPSCs and Differentiation Into Functional Cardiac Fibroblasts
Frontiers in Cell and Developmental Biology, Vol. 9
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In vivo CRISPR-Cas9 inhibition of hepatic LDH as treatment of primary hyperoxaluria
Molecular Therapy - Methods and Clinical Development, Vol. 25, pp. 137-146
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One-Step In Vitro Generation of ETV2-Null Pig Embryos
Animals, Vol. 12, Núm. 14
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SimiC enables the inference of complex gene regulatory dynamics across cell phenotypes
Communications Biology, Vol. 5, Núm. 1
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Targeting the extra domain A of fibronectin for cancer therapy with CAR-T cells
Journal for ImmunoTherapy of Cancer, Vol. 10, Núm. 8
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Time 2EVOLVE: predicting efficacy of engineered T-cells - how far is the bench from the bedside?
Journal for immunotherapy of cancer, Vol. 10, Núm. 5
2021
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Online monitoring of hiPSC expansion and hepatic differentiation in 3D culture by dielectric spectroscopy
Biotechnology and Bioengineering, Vol. 118, Núm. 9, pp. 3610-3617
2020
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Effect of heart ischemia and administration route on biodistribution and transduction efficiency of AAV9 vectors
Journal of Tissue Engineering and Regenerative Medicine, Vol. 14, Núm. 1, pp. 123-134
2019
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Preclinical Evaluation of a Cell-Based Gene Therapy Using the Sleeping Beauty Transposon System in Choroidal Neovascularization
Molecular Therapy - Methods and Clinical Development, Vol. 15, pp. 403-417
2018
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CRISPR/Cas9-mediated glycolate oxidase disruption is an efficacious and safe treatment for primary hyperoxaluria type I
Nature Communications, Vol. 9, Núm. 1
2017
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Discovery of first-in-class reversible dual small molecule inhibitors against G9a and DNMTs in hematological malignancies
Nature Communications, Vol. 8
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Generation of Macaca fascicularis iPS cell line ATCi-MF1 from adult skin fibroblasts using non-integrative Sendai viruses
Stem Cell Research, Vol. 21, pp. 1-4
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Long-Term PEDF Release in Rat Iris and Retinal Epithelial Cells after Sleeping Beauty Transposon-Mediated Gene Delivery
Molecular Therapy - Nucleic Acids, Vol. 9, pp. 1-11