Publicaciones en las que colabora con Delia D'Avola (5)

2020

  1. Brain ventricular enlargement in human and murine acute intermittent porphyria

    Human molecular genetics, Vol. 29, Núm. 19, pp. 3211-3223

2016

  1. Phase I open label liver-directed gene therapy clinical trial for acute intermittent porphyria

    Journal of Hepatology, Vol. 65, Núm. 4, pp. 776-783

  2. Prospect and progress of gene therapy in acute intermittent porphyria

    Expert Opinion on Orphan Drugs, Vol. 4, Núm. 7, pp. 711-717

  3. Recombinant AAV Integration Is Not Associated with Hepatic Genotoxicity in Nonhuman Primates and Patients

    Molecular Therapy, Vol. 24, Núm. 6, pp. 1100-1105

2013

  1. Safety and liver transduction efficacy of raav5-cohpbgd in nonhuman primates: A potential therapy for acute intermittent porphyria

    Human Gene Therapy, Vol. 24, Núm. 12, pp. 1007-1017