Publications in collaboration with researchers from University of Paris-Sorbonne (2)

2025

  1. Systemic messenger RNA replacement therapy is effective in a novel clinically relevant model of acute intermittent porphyria developed in non-human primates

    Gut, Vol. 74, Núm. 2, pp. 270-283

2024

  1. Exploring current and emerging therapies for porphyrias

    Liver International, Vol. 44, Núm. 9, pp. 2174-2190