Sustained enzymatic correction by rAAV-mediated liver gene therapy protects against induced motor neuropathy in acute porphyria mice

  1. Unzu, C.
  2. Sampedro, A.
  3. Mauleón, I.
  4. Alegre, M.
  5. Beattie, S.G.
  6. De Salamanca, R.E.
  7. Snapper, J.
  8. Twisk, J.
  9. Petry, H.
  10. González-Aseguinolaza, G.
  11. Artieda, J.
  12. Rodríguez-Pena, M.S.
  13. Prieto, J.
  14. Fontanellas, A.
Zeitschrift:
Molecular Therapy

ISSN: 1525-0024,  1525-0016

Datum der Publikation: 2011

Ausgabe: 19

Nummer: 2

Seiten: 243-250

Art: Artikel

DOI: 10.1038/MT.2010.210 GOOGLE SCHOLAR lock_openOpen Access editor
Datenquelle: Scopus