Sustained enzymatic correction by rAAV-mediated liver gene therapy protects against induced motor neuropathy in acute porphyria mice

  1. Unzu, C.
  2. Sampedro, A.
  3. Mauleón, I.
  4. Alegre, M.
  5. Beattie, S.G.
  6. De Salamanca, R.E.
  7. Snapper, J.
  8. Twisk, J.
  9. Petry, H.
  10. González-Aseguinolaza, G.
  11. Artieda, J.
  12. Rodríguez-Pena, M.S.
  13. Prieto, J.
  14. Fontanellas, A.
Revue:
Molecular Therapy

ISSN: 1525-0024,  1525-0016

Année de publication: 2011

Volumen: 19

Número: 2

Pages: 243-250

Type: Article

DOI: 10.1038/MT.2010.210 GOOGLE SCHOLAR lock_openAccès ouvert editor
La source de données: Scopus