mRNA-based therapy in a rabbit model of variegate porphyria offers new insights into the pathogenesis of acute attacks

  1. Jericó, D.
  2. Córdoba, K.M.
  3. Jiang, L.
  4. Schmitt, C.
  5. Morán, M.
  6. Sampedro, A.
  7. Alegre, M.
  8. Collantes, M.
  9. Santamaría, E.
  10. Alegre, E.
  11. Culerier, C.
  12. de Mendoza, A.E.-H.
  13. Oyarzabal, J.
  14. Martín, M.A.
  15. Peñuelas, I.
  16. Ávila, M.A.
  17. Gouya, L.
  18. Martini, P.G.V.
  19. Fontanellas, A.
Journal:
Molecular Therapy - Nucleic Acids

ISSN: 2162-2531

Year of publication: 2021

Volume: 25

Pages: 207-219

Type: Article

DOI: 10.1016/J.OMTN.2021.05.010 GOOGLE SCHOLAR lock_openOpen access editor