mRNA-based therapy in a rabbit model of variegate porphyria offers new insights into the pathogenesis of acute attacks

  1. Jericó, D.
  2. Córdoba, K.M.
  3. Jiang, L.
  4. Schmitt, C.
  5. Morán, M.
  6. Sampedro, A.
  7. Alegre, M.
  8. Collantes, M.
  9. Santamaría, E.
  10. Alegre, E.
  11. Culerier, C.
  12. de Mendoza, A.E.-H.
  13. Oyarzabal, J.
  14. Martín, M.A.
  15. Peñuelas, I.
  16. Ávila, M.A.
  17. Gouya, L.
  18. Martini, P.G.V.
  19. Fontanellas, A.
Aldizkaria:
Molecular Therapy - Nucleic Acids

ISSN: 2162-2531

Argitalpen urtea: 2021

Alea: 25

Orrialdeak: 207-219

Mota: Artikulua

DOI: 10.1016/J.OMTN.2021.05.010 GOOGLE SCHOLAR lock_openSarbide irekia editor