Enhanced AAV transduction across preclinical CNS models: A comparative study in human brain organoids with cross-species evaluations

  1. Drouyer, M.
  2. Merjane, J.
  3. Nedelkoska, T.
  4. Westhaus, A.
  5. Scott, S.
  6. Lee, S.
  7. Burke, P.G.R.
  8. McMullan, S.
  9. Lanciego, J.L.
  10. Vicente, A.F.
  11. Bugallo, R.
  12. Unzu, C.
  13. González-Aseguinolaza, G.
  14. Gonzalez-Cordero, A.
  15. Lisowski, L.
Revista:
Molecular Therapy Nucleic Acids

ISSN: 2162-2531

Any de publicació: 2024

Volum: 35

Número: 3

Tipus: Article

DOI: 10.1016/J.OMTN.2024.102264 GOOGLE SCHOLAR lock_openAccés obert editor