Enhanced AAV transduction across preclinical CNS models: A comparative study in human brain organoids with cross-species evaluations

  1. Drouyer, M.
  2. Merjane, J.
  3. Nedelkoska, T.
  4. Westhaus, A.
  5. Scott, S.
  6. Lee, S.
  7. Burke, P.G.R.
  8. McMullan, S.
  9. Lanciego, J.L.
  10. Vicente, A.F.
  11. Bugallo, R.
  12. Unzu, C.
  13. González-Aseguinolaza, G.
  14. Gonzalez-Cordero, A.
  15. Lisowski, L.
Revue:
Molecular Therapy Nucleic Acids

ISSN: 2162-2531

Année de publication: 2024

Volumen: 35

Número: 3

Type: Article

DOI: 10.1016/J.OMTN.2024.102264 GOOGLE SCHOLAR lock_openAccès ouvert editor