Systemic messenger RNA replacement therapy is effective in a novel clinically relevant model of acute intermittent porphyria developed in non-human primates

  1. Córdoba, K.M.
  2. Jericó, D.
  3. Jiang, L.
  4. Collantes, M.
  5. Alegre, M.
  6. García-Ruiz, L.
  7. Manzanilla, O.
  8. Sampedro, A.
  9. Herranz, J.M.
  10. Insausti, I.
  11. Martinez De La Cuesta, A.
  12. Urigo, F.
  13. Alcaide, P.
  14. Morán, M.
  15. Martín, M.A.
  16. Lanciego, J.L.
  17. Lefebvre, T.
  18. Gouya, L.
  19. Quinconces, G.
  20. Unzu, C.
  21. Hervas-Stubbs, S.
  22. Falcón-Pérez, J.M.
  23. Alegre, E.
  24. Aldaz, A.
  25. Fernández-Seara, M.A.
  26. Peñuelas, I.
  27. Berraondo, P.
  28. Martini, P.G.V.
  29. Avila, M.A.
  30. Fontanellas, A.
  31. Show all authors +
Journal:
Gut

ISSN: 1468-3288,  0017-5749

Year of publication: 2024

Type: Article

DOI: 10.1136/GUTJNL-2024-332619 GOOGLE SCHOLAR lock_openOpen access editor
Data source: Scopus