Systemic messenger RNA replacement therapy is effective in a novel clinically relevant model of acute intermittent porphyria developed in non-human primates

  1. Córdoba, K.M.
  2. Jericó, D.
  3. Jiang, L.
  4. Collantes, M.
  5. Alegre, M.
  6. García-Ruiz, L.
  7. Manzanilla, O.
  8. Sampedro, A.
  9. Herranz, J.M.
  10. Insausti, I.
  11. Martinez De La Cuesta, A.
  12. Urigo, F.
  13. Alcaide, P.
  14. Morán, M.
  15. Martín, M.A.
  16. Lanciego, J.L.
  17. Lefebvre, T.
  18. Gouya, L.
  19. Quinconces, G.
  20. Unzu, C.
  21. Hervas-Stubbs, S.
  22. Falcón-Pérez, J.M.
  23. Alegre, E.
  24. Aldaz, A.
  25. Fernández-Seara, M.A.
  26. Peñuelas, I.
  27. Berraondo, P.
  28. Martini, P.G.V.
  29. Avila, M.A.
  30. Fontanellas, A.
  31. Erakutsi egile guztiak +
Aldizkaria:
Gut

ISSN: 1468-3288,  0017-5749

Argitalpen urtea: 2024

Mota: Artikulua

DOI: 10.1136/GUTJNL-2024-332619 GOOGLE SCHOLAR lock_openSarbide irekia editor
Datuen iturria: Scopus