Sustained enzymatic correction by rAAV-mediated liver gene therapy protects against induced motor neuropathy in acute porphyria mice

  1. Unzu, C.
  2. Sampedro, A.
  3. Mauleón, I.
  4. Alegre, M.
  5. Beattie, S.G.
  6. De Salamanca, R.E.
  7. Snapper, J.
  8. Twisk, J.
  9. Petry, H.
  10. González-Aseguinolaza, G.
  11. Artieda, J.
  12. Rodríguez-Pena, M.S.
  13. Prieto, J.
  14. Fontanellas, A.
Journal:
Molecular Therapy

ISSN: 1525-0024 1525-0016

Year of publication: 2011

Volume: 19

Issue: 2

Pages: 243-250

Type: Article

DOI: 10.1038/MT.2010.210 GOOGLE SCHOLAR lock_openOpen access editor

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