Sustained enzymatic correction by rAAV-mediated liver gene therapy protects against induced motor neuropathy in acute porphyria mice
- Unzu, C.
- Sampedro, A.
- Mauleón, I.
- Alegre, M.
- Beattie, S.G.
- De Salamanca, R.E.
- Snapper, J.
- Twisk, J.
- Petry, H.
- González-Aseguinolaza, G.
- Artieda, J.
- Rodríguez-Pena, M.S.
- Prieto, J.
- Fontanellas, A.
ISSN: 1525-0024, 1525-0016
Year of publication: 2011
Volume: 19
Issue: 2
Pages: 243-250
Type: Article